GENE THERAPY FOR RARE DISEASE MARKET SIZE AND SHARE ANALYSIS - GROWTH TRENDS AND FORECASTS (2024 - 2031)

Table of Contents (Version-2026)

1. Research Objective and assumption

• Research Objectives
• Assumptions
• Abbreviations

2. Market Purview

• Report Description
• Market Definition and Scope
• Executive Summary
• Market Snippet, By Drug
• Market Snippet, By Therapeutic Application
• Market Snippet, By Region
• Coherent Opportunity Map (COM)

3. Market Dynamics, Regulations, and Trends Analysis

• Market Dynamics
• Drivers
• Restraints
• Market Opportunities
• PEST Analysis
• PORTER’s Five Forces Analysis
• Regulatory Scenario
• Reimbursement Scenario
• Product Launches
• Partnership & Collaboration Scenario
• Pipeline Analysis
• Investment Scenario
• Epidemiology

4. Global Gene Therapy for Rare Disease Market, By Drug, 2018–2026 (US$ Mn)

• Introduction
• Market Share Analysis, 2017 and 2026 (%)
• Y-o-Y Growth Analysis, 2018–2026
• Segment Trends
• Approved Drugs
• Introduction
• Market Size and Forecast, and Y-o-Y Growth, 2016–2026, (US$ Mn)
• Tisagenlecleucel (Kymriah)
• Axicabtagene ciloleucel (Yescarta)
• Voretigene neparvovec (Luxturna)
• Strimvelis
• Pipeline Drugs
• Introduction
• Market Size and Forecast, and Y-o-Y Growth, 2016–2026, (US$ Mn)
• GT-AADC
• Fidanacogene elaparvovec (SPK-9011)
• OTL-200
• bb2121
• AMT-061
• Others

5. Global Gene Therapy for Rare Disease Market, By Therapeutic Application, 2018–2026 (US$ Mn)

• Introduction
• Market Share Analysis, 2017 and 2026 (%)
• Y-o-Y Growth Analysis, 2018–2026
• Segment Trends
• Oncology
• Introduction
• Market Size and Forecast, and Y-o-Y Growth, 2016–2026, (US$ Mn)
• Neurological Disorders
• Introduction
• Market Size and Forecast, and Y-o-Y Growth, 2016–2026, (US$ Mn)
• Ophthalmic Disorders
• Introduction
• Market Size and Forecast, and Y-o-Y Growth, 2016–2026, (US$ Mn)
• Hematological Disorders
• Introduction
• Market Size and Forecast, and Y-o-Y Growth, 2016–2026, (US$ Mn)
• Immunodeficiency Disorders
• Introduction
• Market Size and Forecast, and Y-o-Y Growth, 2016–2026, (US$ Mn)
• Metabolic Disorders
• Introduction
• Market Size and Forecast, and Y-o-Y Growth, 2016–2026, (US$ Mn)
• Others        
• Introduction
• Market Size and Forecast, and Y-o-Y Growth, 2016–2026, (US$ Mn)

6. Global Gene Therapy for Rare Disease Market, By Regions, 2018–2026 (US$ Mn)

• Introduction
• Market Share Analysis, By Region, 2017 and 2026 (%)
• Y-o-Y Growth Analysis, For Regions, 2018–2026
• North America
• Market Size and Forecast, By Drug, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Therapeutic Application, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Country, 2018–2026 (US$ Mn)
• U.S.
• Canada
• Europe
• Market Size and Forecast, By Drug, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Therapeutic Application, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Country, 2018–2026 (US$ Mn)
• Germany
• Italy
• France
• Spain
• Russia
• Rest of Europe
• Asia Pacific
• Market Size and Forecast, By Drug, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Therapeutic Application, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Country, 2018–2026 (US$ Mn)
• China
• India
• Japan
• ASEAN
• Australia
• South Korea
• Rest of APAC
• Latin America
• Market Size and Forecast, By Drug, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Therapeutic Application, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Country, 2018–2026 (US$ Mn)
• Brazil
• Mexico
• Argentina
• Rest of Latin America
• Africa
• Market Size and Forecast, By Drug, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Therapeutic Application, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Country, 2018–2026 (US$ Mn)
• Central Africa
• South Africa
• North Africa
• Middle East
• Market Size and Forecast, By Drug, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Therapeutic Application, 2018–2026 (US$ Mn)
• Market Size and Forecast, By Country, 2018–2026 (US$ Mn)
• GCC
• Israel
• Rest of Middle East

7. Competitive Landscape

• Heat Map Analysis
• Company Profiles
• Kite Pharma, Inc. (Gilead Sciences, Inc.)
• Company Overview
• Product Portfolio
• Key Developments
• Financial Performance
• Strategies
• Novartis International AG
• Company Overview
• Product Portfolio
• Key Developments
• Financial Performance
• Strategies
• Juno Therapeutics Inc. (Celgene Corporation)
• Company Overview
• Product Portfolio
• Key Developments
• Financial Performance
• Strategies
• Bluebird Bio, Inc.
• Company Overview
• Product Portfolio
• Key Developments
• Financial Performance
• Strategies
• Spark Therapeutics, Inc.
• Company Overview
• Product Portfolio
• Key Developments
• Financial Performance
• Strategies
• uniQure N.V
• Company Overview
• Product Portfolio
• Key Developments
• Financial Performance
• Strategies
• Orchard Therapeutics Plc.
• Company Overview
• Product Portfolio
• Key Developments
• Financial Performance
• Strategies
• PTC Therapeutics Inc.
• Company Overview
• Product Portfolio
• Key Developments
• Financial Performance
• Strategies
• BioMarin Pharmaceutical Inc.
• Company Overview
• Product Portfolio
• Key Developments
• Financial Performance
• Strategies  

8. Section

• References
• Research Methodology
• About us and Sales Contact

*Browse 26 market data tables and 37 figures on "Gene Therapy for Rare Diseases Market - Global forecast to 2026”.